HDBUZZ.NET
Catching a Giant Protein: Five New Ways to Grab Huntingtin
Huntington’s disease (HD) is caused by a change in a single gene known as huntingtin. This gene contains the instructions for making the huntingtin protein. Despite more than three decades passing since the HD gene was discovered, scientists are still trying to figure out exactly what the huntingtin protein does in healthy cells, and how the HD version causes disease. Read full article here
By Dr Rachel Harding & Dr Sarah Hernandez
June 17, 2026
The Other Shoe Drops: uniQure Shares Plans To Submit Licensing Application With The FDA for AMT-130
“After a turbulent past year, uniQure have shared encouraging news that the FDA has agreed their Phase I/II study data can serve as the basis for an application that could lead to the approval of AMT-130 in the US.”
Read the full article: https://en.hdbuzz.net/the-
June 23, 2026
Norvartis-A Study to Investigate the Efficacy, Safety and Tolerability of Votoplam in Participants With Huntington’s Disease
_____________________________________________________________________________________________
Bi-Monthly Advocacy Newsletter: Visit HDSA.org/Takeaction to read the New Bi-Monthly Advocacy Newsletter for updates.