In case you missed uniQure announcement regarding AMT-130, I’m posting the great news for the Huntington’s Disease community around the world. One of the locations for a clinical for AMT-130 is Ohio State.
~ Milestone Marks the First-in-Human AAV Gene Therapy Trial for Huntington’s Disease ~ Lexington, MA and Amsterdam, the Netherlands, June 19, 2020 —
uniQure N.V. (NASDAQ: QURE), a leading gene therapy company advancing transformative therapies for patients with severe medical needs, today announced that the first two patients in the Phase I/II clinical trial of AMT-130 for the treatment of Huntington’s disease have been treated. To read the complete news release, visit: AMT-130_Huntingtons_Disease_FINAL.pdf
I’m a Huntington’s disease advocate, the Chair for HDSA San Francisco Bay Area Affiliate, a blogger and the author of the nonfiction book, Watching Their Dance: Three Sisters, a Genetic Disease and Marrying into a Family At Risk for Huntington’s.
John and I have donated 100% of the profit from the book to the nonprofit, Huntington’s Disease Society of America (HDSA). To date, we’ve gifted over $15,000.00. Review by Goodreads: Goodreads.com-Watching-Their-Dance
My family wants to see the eradication of this horrific disease that has devastated the Marin Family for generations.
We Can Never Lose HOPE……………